KHAN, Dr. Sofia. Gene Therapy in Rare Diseases: Clinical and Translational Perspectives. Academia International Research Journal (Multi Disciplinary), [S. l.], v. 1, n. 1, p. 17–32, 2025. DOI: 10.63056/airj.1.1.2025.609. Disponível em: https://academia.edu.pk/index.php/AIRJ/article/view/609. Acesso em: 14 aug. 2026.